학술논문
Outcomes of Gene Therapy for Severe Sickle Disease and Beta-Thalassemia Major Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral Beta AT87Q-Globin Vector
Document Type
Abstract
Author
Cavazzana, Marina; Ribeil, Jean-Antoine ; Payen, Emmanuel ; Suarez, Felipe; Beuzard, Yves ; Touzot, Fabien ; Cavallesco, Resy; Lefrere, Francois ; Chretien, Stany ; Bourget, Philippe ; Monpoux, Fabrice ; Pondarre, Corinne ; Neven, Benedicte ; Schmidt, Manfred ; von Kalle, Christof ; Kuypers, Frans A.; Sandler, Laura ; Soni, Sandeep; Hermine, Olivier ; Blanche, Stephane ; De Montalembert, Mariane; Hacien-Bey-Abina, Salima ; Leboulch, Philippe
Source
In Blood 3 December 2015 126(23):202-202
Subject
Language
ISSN
0006-4971