학술논문
Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B): 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial
Document Type
Article
Author
Castaman, Giancarlo; Crary, Shelley E; Escobar, Miguel; Gomez, Esteban; Haley, Kristina M; Hermans, Cedric R J R; Kampmann, Peter; Kazmi, Rashid; Key, Nigel S; Klamroth, Robert; Konkle, Barbara A; Kruse-Jarres, Rebecca; Lattimore, Susan; Lemons, Richard; Meijer, Karina; O'Connell, Niamh; Quon, Doris V; Raheja, Priyanka; Symington, Emily; Verhamme, Peter; Visweshwar, Nathan; von Drygalski, Annette; Wang, Michael; Wheeler, Allison P; White, Shanna; Young, Guy; Coppens, Michiel ; Pipe, Steven W; Miesbach, Wolfgang; Astermark, Jan; Recht, Michael; van der Valk, Paul; Ewenstein, Bruce; Pinachyan, Karen; Galante, Nicholas; Le Quellec, Sandra; Monahan, Paul E; Leebeek, Frank W G
Source
In The Lancet Haematology April 2024 11(4):e265-e275
Subject
Language
ISSN
2352-3026