학술논문
Young mice administered adult doses of AAV5-hFVIII-SQ achieve therapeutic factor VIII expression into adulthood
Document Type
Article
Author
Zhang, Lening; Yates, Bridget; Murphy, Ryan; Liu, Su; Xie, Lin; Handyside, Britta; Sihn, Choong-Ryoul; Bouwman, Taren; Galicia, Nicole; Tan, Danielle; Fonck, Carlos; Arens, Jeremy; Clark, Annie; Zhang, Weiming; Chandra, Sundeep; Srimani, Jaydeep; Holcomb, Jennifer; Van Tuyl, Andrea; Henshaw, Joshua; Vettermann, Christian; Siso, Silvia; Su, Cheng; Bullens, Sherry; Bunting, Stuart; O’Neill, Charles; Fong, Sylvia
Source
In Molecular Therapy - Methods & Clinical Development 8 September 2022 26:519-531
Subject
Language
ISSN
2329-0501