학술논문
P142: Efficacy, safety and tolerability of chenodeoxycholic acid in adult patients with cerebrotendinous xanthomatosis (RESTORE): A randomized, placebo-controlled phase 3 study*
Document Type
Abstract
Author
DeBarber, Andrea; Kisanuki, Yaz; Nobrega, Paulo; Himes, Ryan; Jayadev, Suman; Bernat, John; Prakash, Vikram; Gibson, James; Larson, Austin; Sgobbi, Paulo; Murphy, Edward; Fedor, Brian; Po Foo, Cheryl Wong; Dutta, Rana; Imperiale, Michael; Terner-Rosenthal, Jolan; Garner, Will; Vig, Pamela; Duell, P. Barton; Perez, Sarah; Ramdhani, Ritesh; Saute, Jonas
Source
In Genetics in Medicine Open 2024 2 Supplement 1
Subject
Language
ISSN
2949-7744