학술논문
Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
Document Type
Article
Author
Acsadi, Gyula; Baranello, Giovanni; Blaschek, Astrid; Brandsema, John; Brogna, Claudia; Bruno, Claudio; Connolly, Anne; de Groot, Imelda; De Waele, Liesbeth; Finanger, Erika; Finkel, Richard; Gidaro, Teresa; Guglieri, Michaela; Harper, Amy; Lopez Lobato, Mercedes; Madruga Garrido, Marcos; Magri, Francesca; Manousakis, Georgios; Masson, Riccardo; Monduy, Migvis; Muelas Gomez, Nuria; Munell, Francina; Nascimento, Andres; Nevo, Yoram; Pereon, Yann; Phan, Han; Sansone, Valeria; Scoto, Mariacristina; Vucinic, Dragana; Willis, Tracey; Mercuri, Eugenio ; Vilchez, Juan J; Boespflug-Tanguy, Odile; Zaidman, Craig M; Mah, Jean K; Goemans, Nathalie; Müller-Felber, Wolfgang; Niks, Erik H; Schara-Schmidt, Ulrike; Bertini, Enrico; Comi, Giacomo P; Mathews, Katherine D; Servais, Laurent; Vandenborne, Krista; Johannsen, Jessika; Messina, Sonia; Spinty, Stefan; McAdam, Laura; Selby, Kathryn; Byrne, Barry; Laverty, Chamindra G; Carroll, Kevin; Zardi, Giulia; Cazzaniga, Sara; Coceani, Nicoletta; Bettica, Paolo; McDonald, Craig M
Source
In The Lancet Neurology April 2024 23(4):393-403
Subject
Language
ISSN
1474-4422