학술논문
Lentiviral hematopoietic stem cell gene therapy (atidarsagene autotemcel) for late juvenile metachromatic leukodystrophy (MLD)
Document Type
Abstract
Author
Gallo, Vera; Calbi, Valeria; De Mattia, Fabiola; Zambon, Alberto Andrea; Recupero, Salvatore; Fratini, Elena Sophia; Ciotti, Francesca; Fraschini, Maddalena; Sangalli, Mara; Sarzana, Marina; Clerici, Alessandra; Morena, Francesco; Martino, Sabata; Brooks, Jean; Richardson, Alan; Campbell, Laura; Aiuti, Alessandro; Fumagalli, Francesca
Source
In Molecular Genetics and Metabolism February 2024 141(2)
Subject
Language
ISSN
1096-7192