학술논문
Longitudinal natural history studies based on real-world data in rare diseases: Opportunity and a novel approach
Document Type
Review Article
Author
Adang, Laura Ann; Sevagamoorthy, Anjana; Sherbini, Omar; Fraser, Jamie L.; Bonkowsky, Joshua L.; Gavazzi, Francesco; D'Aiello, Russel; Modesti, Nicholson B.; Yu, Emily; Mutua, Sylvia; Kotes, Emma; Shults, Justine; Vincent, Ariel; Emrick, Lisa T.; Keller, Stephanie; Van Haren, Keith P.; Woidill, Sarah; Barcelos, Isabella; Pizzino, Amy; Schmidt, Johanna L.; Eichler, Florian; Fatemi, Ali; Vanderver, Adeline
Source
In Molecular Genetics and Metabolism May 2024 142(1)
Subject
Language
ISSN
1096-7192