학술논문
Treatment of infantile-onset Pompe disease in a rat model with muscle-directed AAV gene therapy
Document Type
Article
Author
Muñoz, Sergio; Bertolin, Joan; Jimenez, Veronica; Jaén, Maria Luisa; Garcia, Miquel; Pujol, Anna; Vilà, Laia; Sacristan, Victor; Barbon, Elena; Ronzitti, Giuseppe; El Andari, Jihad; Tulalamba, Warut; Pham, Quang Hong; Ruberte, Jesus; VandenDriessche, Thierry; Chuah, Marinee K.; Grimm, Dirk; Mingozzi, Federico; Bosch, Fatima
Source
In Molecular Metabolism March 2024 81
Subject
Language
ISSN
2212-8778