학술논문
Lentiviral Hematopoietic Stem and Progenitor Cell Gene Therapy for Wiskott-Aldrich Syndrome (WAS): Up to 8 Years of Follow up in 17 Subjects Treated Since 2010
Document Type
Abstract
Author
Ferrua, Francesca ; Cicalese, Maria Pia ; Galimberti, Stefania ; Giannelli, Stefania ; Dionisio, Francesca ; Barzaghi, Federica ; Migliavacca, Maddalena ; Bernardo, Maria Ester ; Calbi, Valeria ; Tucci, Francesca ; Assanelli, Andrea A. ; Peccatori, Jacopo ; Albertazzi, Elena ; Clerici, Alessandra G. ; Salerio, Federica A. ; Scala, Serena ; Basso-Ricci, Luca ; Cenciarelli, Sabina ; Canarutto, Daniele ; Fraschetta, Federico ; Bartoli, Antonella ; Wolf, Hermann M. ; Silvani, Paolo ; Gattillo, Salvatore ; Coppola, Milena ; Santoleri, Luca ; Villa, Anna ; Jones, Russell ; Dott, Chris ; Grazia Valsecchi, Maria ; Ciceri, Fabio ; Naldini, Luigi ; Aiuti, Alessandro
Source
In Blood 13 November 2019 134 Supplement 1:3346-3346
Subject
Language
ISSN
0006-4971