학술논문
Lentivirus-mediated gene therapy corrects ribosomal biogenesis and shows promise for Diamond Blackfan anemia
Document Type
Article
Author
Giménez, Y.; Palacios, M.; Sánchez-Domínguez, R.; Peral, J.; Ugalde, L.; Alberquilla, O.; Villanueva, M.; Río, P.; Segovia, J.C.; Bueren, J.; Navarro, S.; Beléndez, C.; Zorbas, C.; Lafontaine, D.L.J.; Puzik, A.; Strahm, B.; Niemeyer, C.M.; Gálvez, E.; Sevilla, J.; Da Costa, L.; Strullu, M.; Leblanc, T.; Catala, A.; Ruiz-Llobet, A.
Source
In: JCI Insight . (JCI Insight, 22 May 2024, 9(10))
Subject
Language
English
ISSN
23793708