학술논문
Clinical spectrum of pyruvate kinase deficiency: Data from the pyruvate kinase deficiency natural history study
Document Type
Article
Author
Bianchi, P.; Fermo, E.; Zanella, A.; Barcellini, W.; van Beers, E.J.; Eber, S.W.; Glader, B.; Yaish, H.M.; Despotovic, J.M.; Rothman, J.A.; Sharma, M.; McNaull, M.M.; Lezon-Geyda, K.; Gallagher, P.G.; Morton, D.H.; Neufeld, E.J.; Wang, W.C.; Chonat, S.; Kollmar, N.; Knoll, C.M.; Kuo, K.; Kwiatkowski, J.L.; Pospíšilová, D.; Pastore, Y.D.; Thompson, A.A.; Newburger, P.E.; Ravindranath, Y.; Wlodarski, M.W.; Wang, H.; Holzhauer, S.; Breakey, V.R.; Kunz, J.; Sheth, S.; Rose, M.J.; Bradeen, H.A.; Grace, R.F.; Neu, N.; Guo, D.; Al-Sayegh, H.; London, W.B.
Source
In: Blood . (Blood, 17 May 2018, 131(20):2183-2192)
Subject
Language
English
ISSN
15280020
00064971
00064971