학술논문

Long-term benefit of enzyme replacement therapy with alglucosidase alfa in adults with Pompe disease: Prospective analysis from the French Pompe Registry
Document Type
Article
Source
In: Journal of Inherited Metabolic Disease. (Journal of Inherited Metabolic Disease, November 2020, 43(6):1219-1231)
Subject
Language
English
ISSN
15732665
01418955