학술논문
Intrathecal Gene Therapy for Giant Axonal Neuropathy
Document Type
Article
Author
Bharucha-Goebel, D.X.; Todd, J.J.; Saade, D.; Foley, A.R.; Mohassel, P.; Bönnemann, C.G.; Norato, G.; Lehky, T.; Heiss, J.D.; Jain, M.; Waite, M.; Zein, W.M.; Huryn, L.A.; Kang, E.M.; Crawford, T.O.; Sumner, C.J.; Hoke, A.; Bailey, R.M.; Gray, S.J.; Tesfaye, E.; Chichester, J.A.; Carlin, B.P.; Seremula, B.; Calcedo, R.; Charnas, L.; Rybin, D.; Armao, D.; Bouldin, T.W.; Hooper, J.E.
Source
In: New England Journal of Medicine . (New England Journal of Medicine, 21 March 2024, 390(12):1092-1104)
Subject
Language
English
ISSN
15334406
00284793
00284793