학술논문
Functional restoration of a CFTR splicing mutation through RNA delivery of CRISPR adenine base editor
Document Type
Article
Author
Source
In: Molecular Therapy , Special issue on harnessing the power of noncoding RNAs as tools and targets in gene therapy. (Molecular Therapy, 7 June 2023, 31(6):1647-1660)
Subject
Language
English
ISSN
15250024
15250016
15250016