학술논문
Rycal S48168 (ARM210) for RYR1-related myopathies: a phase one, open-label, dose-escalation trial
Document Type
Article
Author
Todd, J.J.; Brooks, K.; Mendoza, C.J.; Foley, A.R.; Bönnemann, C.G.; Mohassel, P.; Lawal, T.A.; Chrismer, I.C.; Pocock, S.; Riekhof, W.; Varma, P.; Emile-Backer, M.; Meilleur, K.G.; Norato, G.; Kokkinis, A.; Grunseich, C.; Jain, M.S.; Waite, M.R.; Biancavilla, V.; Cheung, K.; Colina-Prisco, C.; Marks, A.R.; Webb, Y.; Marcantonio, E.E.
Source
In: eClinicalMedicine . (eClinicalMedicine, February 2024, 68)
Subject
Language
English
ISSN
25895370