학술논문
Genetically corrected RAG2-SCID human hematopoietic stem cells restore V(D)J-recombinase and rescue lymphoid deficiency
Document Type
Article
Author
Pavel-Dinu, M.; Viel, S.; Ghanim, H.Y.; Sheikali, A.; Menezes, S.T.; Chrobok, J.; Hernández González, E.M.; Porteus, M.H.; Gardner, C.L.; Kawai, T.; Delmonte, O.M.; Palterer, B.; Bosticardo, M.; Pala, F.; Notarangelo, L.D.; Nakauchi, Y.; Majeti, R.; Malech, H.L.; Bode, N.M.; Kurgan, G.L.; Vakulskas, C.A.; Detweiler, A.M.; Neff, N.F.
Source
In: Blood Advances . (Blood Advances, 9 April 2024, 8(7):1820-1833)
Subject
Language
English
ISSN
24739537
24739529
24739529