학술논문

Increase in Full-Length Dystrophin by Exon Skipping in Duchenne Muscular Dystrophy Patients with Single Exon Duplications: An Open-label Study
Document Type
Article
Source
In: Journal of Neuromuscular Diseases. (Journal of Neuromuscular Diseases, 30 April 2024, 11(3):679-685)
Subject
Language
English
ISSN
22143602
22143599