학술논문
Increase in Full-Length Dystrophin by Exon Skipping in Duchenne Muscular Dystrophy Patients with Single Exon Duplications: An Open-label Study
Document Type
Article
Author
Source
In: Journal of Neuromuscular Diseases . (Journal of Neuromuscular Diseases, 30 April 2024, 11(3):679-685)
Subject
Language
English
ISSN
22143602
22143599
22143599