학술논문

The Clinical Development of Taldefgrobep Alfa: An Anti-Myostatin Adnectin for the Treatment of Duchenne Muscular Dystrophy
Document Type
Article
Author
Muntoni, F.Byrne, B.J.McMillan, H.J.Ryan, M.M.Wong, B.L.Dukart, J.Bansal, A.Cosson, V.Dreghici, R.Guridi, M.Wagner, K.R.Rabbia, M.Yen, K.Staunton, H.Tirucherai, G.S.Yuan, X.Carvajal, I.Chimalakonda, A.Gokemeijer, J.Gulianello, M.Hellbach, N.Kozhich, A.Kukral, D.Malone, H.Meredith, J.E.Pletcher, M.Rakestraw, G.Schneeweis, L.Swain, J.Zambito, F.Chang, M.Hamuro, L.Luo, F.Peterson, J.E.Hocknell, P.Lou, Z.Madireddi, M.Pletcher, M.Bechtold, C.M.Ahlijanian, M.K.Chang, M.Hamuro, L.Jacobsen, L.K.Kozhich, A.Luo, F.Peterson, J.E.Zambito, F.Kletzl, H.Dubrovsky, A.L.Mesa, L.Chloca, F.Jauregu, A.Jones, K.Ryan, M.Campbell, C.Mah, J.Ho, A.Chiu, A.D’Souza, V.Sadowski, R.Dao, J.Grice, M.Price, T.McMillan, H.Sell, E.McCormick, A.Gidaro, T.Seferian, A.Péréon, Y.Magot, A.Vuillerot, C.Schara-Schmidt, U.Sansone, V.Albamonte, E.Di Bari, A.Refran, J.Salmin, F.Vita, G.Vita, G.L.Consulo, C.Komaki, H.Ishiyama, A.Matsumura, T.Saito, T.Ichihara, K.Hayashi, N.Terada, K.Takehara, K.Hayashi, N.Takeshima, Y.Nascimiento, A.Natera, D.Carrera, L.Exposito, J.Ortez, C.Medina, J.Moya, O.Roca, S.Rodriguez, A.Valle, M.de Groot, I.J.M.Niks, E.H.van Heur-Neuman, M.J.van der Holst, M.Scoto, M.Brusa, C.Afazal, A.Miller, E.Byrne, B.J.Cripe, L.Finkel, R.S.Heydemann, P.Matthews, K.Miller, C.Laubsher, K.Mockeler, S.Phan, H.Sivakumar, K.Osgood, K.Statland, J.Tian, C.Wagner, K.R.Leung, D.Bibat, G.Stinson, N.Servais, L.Mercuri, E.Duong, T.Scoto, M.Campbell, C.Strijbos, P.Veenstra, K.
Source
In: Neurology and Therapy. (Neurology and Therapy, February 2024, 13(1):183-219)
Subject
Language
English
ISSN
21936536
21938253