학술논문
mRNA Therapy Improves Metabolic and Behavioral Abnormalities in a Murine Model of Citrin Deficiency
Document Type
Article
Author
Cao, J.; An, D.; Galduroz, M.; Zhuo, J.; Liang, S.; Eybye, M.; Frassetto, A.; Santana, J.; Mihai, C.; Benenato, K.E.; Kumarasinghe, E.S.; Sabnis, S.; Salerno, T.; Coughlan, K.; Miracco, E.J.; Levy, B.; Besin, G.; Schultz, J.; Lukacs, C.; Guey, L.; Finn, P.; Giangrande, P.H.; Martini, P.G.V.; Kuroda, E.; Funahashi, A.; Furukawa, T.; Saheki, T.
Source
In: Molecular Therapy . (Molecular Therapy, 3 July 2019, 27(7):1242-1251)
Subject
Language
English
ISSN
15250024
15250016
15250016