학술논문
Repeated AAV-mediated gene transfer by serotype switching enables long-lasting therapeutic levels of hUgt1a1 enzyme in a mouse model of Crigler-Najjar Syndrome Type i
Document Type
Article
Author
Source
In: Gene Therapy . (Gene Therapy, 1 October 2017, 24(10):649-660)
Subject
Language
English
ISSN
14765462
09697128
09697128