학술논문
Challenges of Assessing Exon 53 Skipping of the Human DMD Transcript with Locked Nucleic Acid-Modified Antisense Oligonucleotides in a Mouse Model for Duchenne Muscular Dystrophy
Document Type
Article
Author
Source
In: Nucleic Acid Therapeutics . (Nucleic Acid Therapeutics, 1 December 2023, 33(6):348-360)
Subject
Language
English
ISSN
21593345
21593337
21593337