학술논문
mRNA therapy corrects defective glutathione metabolism and restores ureagenesis in preclinical argininosuccinic aciduria
Document Type
Article
Author
Gurung, S.; Perocheau, D.; Gil-Martinez, A.L.; Touramanidou, L.; Khalil, Y.; Spiewak, J.; Ridout, D.; Heywood, W.; Heales, S.; Mills, P.B.; Gissen, P.; Eaton, S.; Ryten, M.; Baruteau, J.; Timmermand, O.V.; Barber, A.R.; Edwards, R.S.; Witney, T.H.; Minnion, M.; Feelisch, M.; Pinto, P.L.; Finn, P.F.; Cavedon, A.; Siddiqui, S.; Rice, L.; Martini, P.G.V.; Frassetto, A.; Hargreaves, I.; Waddington, S.N.; Fang, S.; Messina, M.
Source
In: Science Translational Medicine . (Science Translational Medicine, 2024, 16(729))
Subject
Language
English
ISSN
19466242
19466234
19466234