학술논문

Chemically modified recombinant human sulfamidase (SOBI003) in mucopolysaccharidosis IIIA patients: Results from an open, non-controlled, multicenter study
Document Type
Article
Source
In: Molecular Genetics and Metabolism. (Molecular Genetics and Metabolism, August 2022, 136(4):249-259)
Subject
Language
English
ISSN
10967206
10967192