학술논문
Garetosmab in fibrodysplasia ossificans progressiva: a randomized, double-blind, placebo-controlled phase 2 trial
Document Type
Article
Author
Di Rocco, M.; Madeo, A.; Forleo-Neto, E.; Portal-Celhay, C.; Sarkar, N.; Hou, P.; Musser, B.J.; Boyapati, A.; Mohammadi, K.; Mellis, S.J.; Rankin, A.J.; Economides, A.N.; Trotter, D.G.; Herman, G.A.; O’Meara, S.J.; DelGizzi, R.; Weinreich, D.M.; Yancopoulos, G.D.; Pignolo, R.J.; Keen, R.; Bubbear, J.S.; Orcel, P.; Funck-Brentano, T.; Roux, C.; Kolta, S.; Tabarkiewicz, J.; Szczepanek, M.; Bachiller-Corral, J.; Cheung, A.M.; Tile, L.; Dahir, K.M.; Botman, E.; Eekhoff, E.M.W.; Raijmakers, P.G.; Mukaddam, M.A.; Kaplan, F.S.
Source
In: Nature Medicine . (Nature Medicine, October 2023, 29(10):2615-2624)
Subject
Language
English
ISSN
1546170X
10788956
10788956