학술논문
Widespread and sustained target engagement in Huntington s disease minipigs upon intrastriatal microRNA-based gene therapy
Document Type
Article
Author
Valles, A.; Evers, M.M.; Stam, A.; Gonzalez, M.S.; Brouwers, C.; Tornero, C.V.; Broekmans, S.A.; Paerels, L.; Blits, B.; Petry, H.; Deventer, S.V.; Konstantinova, P.; Klima, J.; Bohuslavova, B.; Ellederova, Z.; Motlik, J.; Pintauro, R.; Fodale, V.; Bresciani, A.; Liscak, R.; Urgosik, D.; Starek, Z.; Crha, M.
Source
In: Science Translational Medicine . (Science Translational Medicine, 7 April 2021, 13(588))
Subject
Language
English
ISSN
19466242
19466234
19466234