학술논문
Safety and efficacy of losmapimod in facioscapulohumeral muscular dystrophy (ReDUX4): a randomised, double-blind, placebo-controlled phase 2b trial
Document Type
Article
Author
Tawil, R.; Hamel, J.I.; Wagner, K.R.; Leung, D.G.; Statland, J.M.; Wang, L.H.; Genge, A.; Sacconi, S.; Lochmüller, H.; Reyes-Leiva, D.; Diaz-Manera, J.; Alonso-Perez, J.; Muelas, N.; Vilchez, J.J.; Pestronk, A.; Gibson, S.; Goyal, N.A.; Hayward, L.J.; Johnson, N.; LoRusso, S.; Freimer, M.; Shieh, P.B.; Subramony, S.H.; van Engelen, B.; Kools, J.; Leinhard, O.D.; Widholm, P.; Morabito, C.; Moxham, C.M.; Cadavid, D.; Mellion, M.L.; Odueyungbo, A.; Tracewell, W.G.; Accorsi, A.; Ronco, L.; Gould, R.J.; Shoskes, J.; Rojas, L.A.; Jiang, J.G.
Source
In: The Lancet Neurology . (The Lancet Neurology, May 2024, 23(5):477-486)
Subject
Language
English
ISSN
14744465
14744422
14744422