학술논문

Preclinical Development of Antisense Oligonucleotides to Rescue Aberrant Splicing Caused by an Ultrarare ABCA4 Variant in a Child with Early-Onset Stargardt Disease
Document Type
Article
Source
In: Cells. (Cells, April 2024, 13(7))
Subject
Language
English
ISSN
20734409