학술논문
CRISPR/Cas9 and piggyBac Transposon-Based Conversion of a Pathogenic Biallelic TBCD Variant in a Patient-Derived iPSC Line Allows Correction of PEBAT-Related Endophenotypes
Document Type
Article
Author
Source
In: International Journal of Molecular Sciences . (International Journal of Molecular Sciences, May 2023, 24(9))
Subject
Language
English
ISSN
14220067
16616596
16616596