학술논문
Optimized allele-specific silencing of the dominant-negative COL6A1 G293R substitution causing collagen VI-related dystrophy
Document Type
Article
Author
Source
In: Molecular Therapy Nucleic Acids . (Molecular Therapy Nucleic Acids, 11 June 2024, 35(2))
Subject
Language
English
ISSN
21622531