학술논문
First-in-Human Gene Therapy Trial of AAV8-hCARp.hCNGB3 in Adults and Children With CNGB3-associated Achromatopsia
Document Type
Article
Author
Michaelides, M.; Zaman, S.; Smith, A.J.; Robson, A.G.; Kane, T.; Georgiou, M.; Kalitzeos, A.; Ali, R.R.; Bainbridge, J.; Hirji, N.; Wong, S.C.; Kumaran, N.; Henderson, R.H.; Besirli, C.G.; Georgiadis, A.; Naylor, S.; Forbes, A.; Ripamonti, C.; Gottlob, I.; Thiadens, A.; Fleck, P.; Anglade, E.; Dong, X.; Capuano, G.; Lu, W.; Berry, P.
Source
In: American Journal of Ophthalmology . (American Journal of Ophthalmology, September 2023, 253:243-251)
Subject
Language
English
ISSN
18791891
00029394
00029394