학술논문

Long-term safety and efficacy of patisiran for hereditary transthyretin-mediated amyloidosis with polyneuropathy: 12-month results of an open-label extension study
Document Type
Article
Author
Adams, D.Polydefkis, M.González-Duarte, A.Wixner, J.Kristen, A.V.Schmidt, H.H.Berk, J.L.Losada López, I.A.Dispenzieri, A.Quan, D.Conceição, I.M.Slama, M.S.Gillmore, J.D.Kyriakides, T.Ajroud-Driss, S.Waddington-Cruz, M.Mezei, M.M.Planté-Bordeneuve, V.Attarian, S.Mauricio, E.Brannagan, T.H.Ueda, M.Aldinc, E.Wang, J.J.White, M.T.Vest, J.Berber, E.Sweetser, M.T.Coelho, T.Vita, G.Rizzo, V.Russo, M.Mazzeo, A.Gentile, L.Brueckner, C.Lazzari, V.Wiesman, J.DeLong, D.Victory, J.Dalton, J.May, J.Gilmore, C.Diallo, S.Delmont, E.Pouget, J.Verschueren, A.Grapperon, A.-M.Campana-Salort, E.Lopes, A.Lamas, F.Neves, C.Castro, J.Pereira, P.Castro, I.Franco, A.Santos, M.O.de Azevedo Coutinho, C.Falcao de Campos, C.Hipólito Reis, A.Correia, N.Perez, J.M.Martins da Silva, A.Alves, C.Cardoso, M.Valdrez, K.Monte, J.R.Pessoa, B.Guimaraes, N.Freitas, M.Ramalho, J.Ferreira, N.Kuzume, D.Tard, C.Waucquier, N.Rougeaux, I.Brice, S.Kasprzyk, E.Elrezzi, E.Meguig, S.Hachulla, E.Gauvain, C.Migaud-Chervy, M.-C.Deplanque, D.Jozefowicz, E.Lebellec, L.Balaya-Gouraya, L.Jehan Lacour, N.Bournane, H.Martin, N.Elabed, M.Sacko, N.Boubrit, Y.Gaouar, A.Rakotondratafika, F.Théaudin-Saliou, M.Cauquil-Michon, C.Labeyrie, C.Not, A.Al-Salameh, A.Lecoq, A.-L.Stephant, M.Echaniz-Laguna, A.Becquemont, L.Beaudonnet, G.Algalarrondo, V.Eliahou, L.Signate, A.Berthelot, E.Inamo, J.Vervoitte, L.Focseneanu, C.Gendre, T.Arrouasse, R.Ayache, S.S.Ernande, L.Le Corvoisier, P.Salhi, H.Choumert, A.Ehinger, V.Ruiz, J.Charlin, C.Megelin, T.Brannagan III, T.H.Fayerman, R.Kim, A.Paras, A.Gonzalez, L.J.Tsang, S.Wajnsztajn, F.Shije, J.Ulane, C.Kleyman, I.Weimer, L.Cioroiu, C.Lambrianides, S.Abu-Manneh, R.Zamba-Papanicolaou, E.Agathangelou, P.Leonidou, E.Tada, S.Fujita, A.Nagai, M.Ando, R.Hosokawa, Y.Yamanishi, Y.Overcash, J.S.Giardino, E.Boyer, L.Dang, L.Le, A.Nguyen, T.Giang, L.Sellers, P.Tran, L.Truong, N.Vinas, M.Hrkman, N.Miller, S.Nguyen, D.Smith, A.Pu, H.Li, S.Vuong, T.Dioso, H.Green, S.Lee, K.Chu, H.Waters, M.Coskun, D.J.Zepeda, K.A.O'Riordan, W.Obici, L.Cortese, A.Lozza, A.Merlini, G.Rosti, V.Sabatelli, M.Bisogni, G.Bernardo, D.Luigetti, M.Di Paolantonio, A.Guglielmino, V.Romano, A.Nienhuis, H.Bulthuis-Kuiper, J.Gerk, O.Ulbricht, H.Taylor, L.Meyle, E.Kleinschmidt, N.Meyrath, D.Noe-Schwenn, S.Meng, U.Bauer, R.aus dem Siepen, F.Hein, S.Takahashi, T.Oshita, T.Koujin, Y.Neshige, S.Nezu, T.Segawa, A.Ueno, H.Morino, H.Campistol, J.M.Rodas Marin, L.M.Blasco Pelicano, J.M.Dávila, L.G.Palacios, M.Pytel Cordoba, V.Guerrero Sola, A.Horga, A.García Feijoo, J.Perez de Isla, L.Marques Júnior, W.Moscardini, M.Litcanov, D.C.Viera Lima, A.F.Rodrigues, L.Marques Coutinho, B.Moreira, C.L.Daccach Marques, V.Munoz Beamud, F.Gragera Martínez, Á.Borrachero, C.Cisneros Barroso, E.Rodríguez Rodríguez, A.Sanz, M.Rigo Oliver, E.González Moreno, J.Gamez Martinez, J.M.Descals, C.Uson, M.Jose Vega, F.Figuerola, A.Montala, C.Dias da Silva, M.Gervais de Santa Rosa, R.Pinto, L.F.Pinto, M.V.Cardoso Berensztejn, A.Barroso, F.Lautre, A.Orellana, L.G.González-Duarte Briseño, M.A.Cárdenas-Soto, K.Jiménez López, B.P.Pérez-Castañeda, S.L.Cantú Brito, C.G.Rivera de la Parra, D.Hernandez Reyes, J.P.del Mar Saniger Alba, M.Criollo Mora, E.Parman, Y.Rezzan, K.J.Sahin, E.Serbest, N.G.Durmus, H.Cakar, A.Tugal Tutkun, N.I.Karamursel, S.Elitok, A.Sirin Inan, N.G.Altinkurt, E.Ye, J.Allen, A.C.Chaudhry, V.Jarrett, R.Bressler, N.Burks, K.L.Liu, Q.Khoshnoodi, M.Judge, D.P.Vista, G.Shah, S.M.Hamaguchi, H.Oda, J.Fukase, E.Taniguchi, I.Oda, T.Endo, H.Shimomura, M.Katanazaka, K.Koto, S.Nakano, T.Scheid, C.Zueiter, A.Pester, L.Walter, D.Özdemir, B.Frenzel, L.F.Holtick, U.Oh, J.Kim, H.J.Shin, H.J.Choi, K.Yamashita, T.Masuda, T.Misumi, Y.Ueda, A.Nakahara, K.Yorita, A.Tsuruhisa, S.Taniwaki, T.Harada, M.Moritaka, T.Sakurada, N.Mauricio, E.A.Baskin, A.Dimberg, E.Fonder, A.Hobbs, M.Russell, S.J.Dyck, P.Gonsalves, W.Leung, N.Witzig, T.E.Zeldenrust, S.R.Hwa, L.Kapoor, P.Kumar, S.K.Lin, Y.Lust, J.A.Rajkumar, V.S.Dingli, D.Gertz, M.A.Go, R.Hayman, S.R.Dalia, S.Carrillo, E.Gorevic, P.Mason, G.Chao, C.-C.Lee, M.-J.Su, J.-J.Hsieh, S.-T.Tsai, L.-K.Yeh, S.-J.Yang, C.-C.Ajroud-Driss, S.A.-D.Casey, P.Joslin, B.C.Freimer, M.Sankey, A.Kenepp, A.Heintzman, S.LoRusso, S.Hokezu, Y.Kim, B.-J.Kim, J.Lee, G.Y.Cho, E.B.Jeon, E.-S.Min, J.-H.Seok, J.M.Lee, H.L.Park, J.H.Sekijima, Y.Miyazawa, C.Kato, N.Kishida, D.Hineno, A.Kodaira, M.Yoshinaga, T.Miyahara, T.Imai, A.Matsumoto, K.Lin, K.-P.Lee, Y.-C.Falk, M.Pilebro, B.Suhr, O.Lindqvist, P.Soderberg, K.Pedrosa-Domellöf, F.Anan, I.Nordh, E.Tournev, I.Zhelyazkova-Glaveeva, S.Cherneva, Z.Sarafov, S.Chamova, T.Cherninkova-Gopina, S.Friebel, F.Zibert, A.Mihailovic, N.Schubert, F.Vorona, E.Lahme, L.Huesing-Kabar, A.Schilling, M.Kabar, I.Martinez-Naharro, A.Chacko, L.Cohen, O.Law, S.Rezk, T.Lachmann, H.J.Blume, B.Dixon, S.Low, S.C.Chan, S.L.Lim, H.E.L.Goh, K.J.Kraus, D.Jack, K.Lopate, G.Zwijack, B.Florence, J.Sommerville, R.B.Stewart, G.Ryder, J.Mekhael, L.Taylor, M.Suan, D.Wells, K.Stone, P.Itoya, A.Owusu-Sekyere, M.Thai, D.Chahine, I.Pedrosa, S.Do, T.H.T.
Source
In: The Lancet Neurology. (The Lancet Neurology, January 2021, 20(1):49-59)
Subject
Language
English
ISSN
14744465
14744422