학술논문
Adenine base editing reduces misfolded protein accumulation and toxicity in alpha-1 antitrypsin deficient patient iPSC-hepatocytes
Document Type
Article
Author
Source
In: Molecular Therapy , Expanding the scale and scope of therapeutic gene editing. (Molecular Therapy, 3 November 2021, 29(11):3219-3229)
Subject
Language
English
ISSN
15250024
15250016
15250016