학술논문

CRISPR/Cas9-Induced (CTG⋅CAG)n Repeat Instability in the Myotonic Dystrophy Type 1 Locus: Implications for Therapeutic Genome Editing
Document Type
Article
Source
In: Molecular Therapy. (Molecular Therapy, 4 January 2017, 25(1):24-43)
Subject
Language
English
ISSN
15250024
15250016