학술논문
P005: Atidarsagene autotemcel (hematopoietic stem cell–gene therapy) preserves cognitive and motor development in metachromatic leukodystrophy with up to 12 years follow-up
Document Type
article
Author
Francesca Fumagalli; Valeria Calbi; Fabiola De Mattia; Alberto Zambon; Vera Gallo; Salvatore Recupero; Elena Sophia Fratini; Alessia Ippolito; Francesca Ciotti; Maddalena Fraschini; Marina Sarzana; Stefano Scarparo; Eugenio Montini; Sara Locatelli; Marcella Facchini; Alessandra Clerici; Francesco Morena; Sabata Martino; Muska Yarzi; Sean Moro; Andrew Shenker; Jean Brooks; Alan Richardson; Leslie Meltzer; Laura Campbell; Alessandro Aiuti
Source
Genetics in Medicine Open, Vol 2, Iss , Pp 100882- (2024)
Subject
Language
English
ISSN
2949-7744