학술논문
OP016: Mini-COMET: Safety and efficacy of ≥97 weeks’ avalglucosidase alfa in infantile-onset Pompe disease participants previously treated with alglucosidase alfa
Document Type
Article
Author
Kronn, David; Davison, James; Brassier, Anaïs; Broomfield, Alexander; Hahn, Si Houn; Kumada, Satoko; Labarthe, François; Ohki, Hirotaka; Prakalapakorn, S. Grace; Haack, Kristina An; Meng, Xianzhang; Sparks, Susan; Tammireddy, Swathi; Wilson, Catherine; Zaher, Atef; Zhou, Tianyue; Chien, Yin-Hsiu; Kishnani, Priya; investigators, On behalf of the Mini-COMET
Source
Genetics in Medicine; March 2022, Vol. 24 Issue: 3, Number 3 Supplement 1 pS348-S349, 2p
Subject
Language
ISSN
10983600; 15300366