학술논문
Preferences for potential benefits and risks for gene therapy in the treatment of sickle cell disease
Document Type
Article
Author
Source
Blood Advances; 20230101, Issue: Preprints
Subject
Language
ISSN
24739529; 24739537
Abstract
•The benefits and risks of gene therapy are currently unclear, so it is key to understand their potential value from the patients’ perspective.•The appeal of gene therapy is evident with most respondents, although those with milder symptoms see other treatment options as viable.