학술논문
Phase 1/2 Study of Lumasiran for Treatment of Primary Hyperoxaluria Type 1
Document Type
Article
Author
Frishberg, Yaacov; Deschênes, Georges; Groothoff, Jaap W.; Hulton, Sally-Anne; Magen, Daniella; Harambat, Jérôme; van’t Hoff, William G.; Lorch, Ulrike; Milliner, Dawn S.; Lieske, John C.; Haslett, Patrick; Garg, Pushkal P.; Vaishnaw, Akshay K.; Talamudupula, Sandeep; Lu, Jiandong; Habtemariam, Bahru A.; Erbe, David V.; McGregor, Tracy L.; Cochat, Pierre; Bandara, Asela; Bowen, Jonathan; Chong, Wei Li; Coates, Simon; De Barr, Patrick; De Beer, Janine; Gayed, Juleen; Hill, Timothy; Kotak, Alex; Ono, Junko; Taubel, Jorg; Thayalan, Meera; Wong, Robynne; Coch, Christoph; Coenen, Martin; Feldkotter, Markus; Heiland, Nils Henning; Hohenadel, Maximilian; Hoppe, Bernd; Kyrieleis, Henriette; Schalk, Gesa; Cooper, Lucy; Gupta, Asheeta; Milford, David; Muorah, Mordi; Bacchetta, Justine; Bernoux, Delphine; Bertholet-Thomas, Aurelia; Cheyssac, Elodie; Portefaix, Aurelie; Ranchin, Bruno; Sellier-Leclerc, Anne-Laure; Llanas, Brigitte; Baudouin, Veronique; Couderc, Anne; Hogan, Julien; Kaguelidou, Florentia; Kwon, Theresa; Maisin, Anne; Sas, David; Becker-Cohen, Rachel; Ben-Shalom, Efrat; Rinat, Choni; Behr, Shimrit Tzvi; Bockenhauer, Detlef; Mansour, Bshara; Pollack, Shirley; Garrelfs, Sander; Oosterveld, Michiel; Moochhala, Shabbir; Walsh, Stephen; Kamesh, Lavanya; Lipkin, Graham
Source
Clinical Journal of The American Society of Nephrology; July 2021, Vol. 16 Issue: 7 p1025-1036, 12p
Subject
Language
ISSN
15559041; 1555905X