학술논문
Safety and Efficacy of CTX001 in Patients with Transfusion-Dependent β-Thalassemia (TDT) or Sickle Cell Disease (SCD): Early Results from the Climb THAL-111 and Climb SCD-121 Studies of Autologous CRISPR-Cas9-Modified CD34+Hematopoietic Stem and Progenitor Cells (HSPCs)
Document Type
Article
Author
Soni, Sandeep; Frangoul, Haydar; Bobruff, Yael; Cappellini, Maria Domenica; Corbacioglu, Selim; Fernandez, Christine Marie; de la Fuente, Josu; Grupp, Stephan; Handgretinger, Rupert; Ho, Tony W.; Imren, Suzan; Kattamis, Antonis; Lekstrom-Himes, Julie; Locatelli, Franco; Lu, Yimeng; Mapara, Markus Y.; Mulcahey, Sarah; de Montalembert, Mariane; Rondelli, Damiano; Shanbhag, Niraj; Sheth, Sujit; Steinberg, Martin H.; Weinstein, Michael; Wu, John; Wall, Donna A.
Source
Transplantation and Cellular Therapy; March 2021, Vol. 27 Issue: 3, Number 3 Supplement 1 pS72-S73, 2p
Subject
Language
ISSN
26666375; 26666367