학술논문
One Year Follow-up on the First Patient Treated with Nula-Cel: An Autologous CRISPR/Cas9 Gene Corrected CD34+ Cell Product to Treat Sickle Cell Disease
Document Type
Article
Author
Shyr, David C; Lowsky, Robert; Miller, Weston; Schroeder, Mark A.; Buchholz, Tonia; Dougall, Kirstin; Intondi, Allison; Charles, Alexandra; Lehrer, Josh; Bouge, Ali; Wolf, Stacey; MacDonald, Blair; Din, Hena; Lerner, Alana; Amoury, Manal; Treusch, Sebastien; Chew, Glen; Silva, Brian; Mashhedi, Haider; Siu, Vincent; Perrone, Ian; Vijay, Twaritha; Jain, Aayami; Krassovsky, Kristina; Matern, William; Lahiri, Premanjali; Rodriguez, Ryan; Skowronski, Jason; Batish, Arpit; Margittai, Dana; Wani, Prachi; Van Horn, Timothy; Flautero, Claudia; Flores, Rosalva; Lee, Jade; Tate, Keri; Roncarolo, Maria-Grazia; Feldman, Steven; DiPersio, John; Porteus, Matthew
Source
Blood; November 2023, Vol. 142 Issue: 1, Number 1 Supplement 1 p5000-5000, 1p
Subject
Language
ISSN
00064971; 15280020
Abstract
Introduction