학술논문
In silico and in vitro evaluation of exonic and intronic off-target effects form a critical element of therapeutic ASO gapmer optimization.
Document Type
Article
Author
Kamola, Piotr J.; Kitson, Jeremy D. A.; Turner, Gemma; Maratou, Klio; Eriksson, Sofie; Panjwani, Aliza; Warnock, Linda C.; Guilloux, Gaelle A. Douillard; Moores, Kitty; Koppe, Emma L.; Wixted, William E.; Wilson, Paul A.; Gooderham, Nigel J.; Gant, Timothy W.; Clark, Kenneth L.; Hughes, Stephen A.; Edbrooke, Mark R.; Parry, Joel D.
Source
Nucleic Acids Research; 10/15/2015, Vol. 43 Issue 18, p8638-8650, 13p
Subject
Language
ISSN
03051048