학술논문
Long-term effectiveness of carglumic acid in patients with propionic acidemia (PA) and methylmalonic acidemia (MMA): a randomized clinical trial.
Document Type
Journal Article
Author
Alfadhel, Majid; Nashabat, Marwan; Saleh, Mohammed; Elamin, Mohammed; Alfares, Ahmed; Al Othaim, Ali; Umair, Muhammad; Ahmed, Hind; Ababneh, Faroug; Al Mutairi, Fuad; Eyaid, Wafaa; Alswaid, Abdulrahman; Alohali, Lina; Faqeih, Eissa; Almannai, Mohammed; Aljeraisy, Majed; Albdah, Bayan; Hussein, Mohamed A.; Rahbeeni, Zuhair; Alasmari, Ali
Source
Subject
Language
ISSN
1750-1172
Abstract