학술논문

Comparing developmental outcomes of children with CLN2 disease receiving cerliponase alfa to a natural history cohort.
Document Type
Article
Source
Molecular Genetics & Metabolism. Feb2021, Vol. 132 Issue 2, pS94-S95. 2p.
Subject
*NATURAL history
*JUVENILE diseases
*AGE
*SYMPTOMS
*ENZYME deficiency
Language
ISSN
1096-7192