학술논문

Evaluation of chenodeoxycholic acid treatment in adult patients with cerebrotendinous xanthomatosis: A randomized, placebo-controlled Phase 3 study (RESTORE).
Document Type
Article
Source
Molecular Genetics & Metabolism. Apr2024, Vol. 141 Issue 4, pN.PAG-N.PAG. 1p.
Subject
*CHENODEOXYCHOLIC acid
*ADULTS
*OLDER patients
Language
ISSN
1096-7192