학술논문

Identification of the hyaluronic acid pathway as a therapeutic target for facioscapulohumeral muscular dystrophy.
Document Type
Article
Source
Science Advances. Dec2019, Vol. 5 Issue 12, p1-12. 12p.
Subject
*FACIOSCAPULOHUMERAL muscular dystrophy
*MYOBLASTS
*SPLICEOSOMES
*HYALURONIC acid
*POLYVINYLIDENE fluoride
Language
ISSN
2375-2548
Abstract
The article presents research reports on Identification of the hyaluronic acid pathway as a therapeutic target for facioscapulohumeral muscular dystrophy. Topics discussed include DUX4 misexpression is not tightly correlated with disease severity; patient-derived disease models are mediated by the signaling molecule hyaluronic acid (HA); and unidentified pathologies including mislocalization of mitochondria.