학술논문

P162 TRANSCRIPTIONAL AND POST-TRANSCRIPTIONAL TARGETING OF FVIII EXPRESSION TO OVERCOME IMMUNOLOGICAL RESPONSES TO GENE THERAPY FOR HEMOPHILIA A.
Document Type
Article
Source
Journal of Hepatology. Apr2014 Supplement, Vol. 60, pS119-S120. 1p.
Subject
*HEMOPHILIA treatment
*HEMOPHILIA
*GENETIC transcription
*GENE expression
*IMMUNE response
*GENE targeting
*STIMULUS & response (Biology)
*GENE therapy
Language
ISSN
0168-8278