학술논문
'학술논문'
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Academic Journal
McDonald, Craig M.; Signorovitch, James; Mercuri, Eugenio; Niks, Erik H.; Wong, Brenda; Fillbrunn, Mirko; Sajeev, Gautam; Yim, Erica; Dieye, Ibrahima; Miller, Debra; Ward, Susan J.; Goemans, Nathalie
Academic Journal
Muntoni, Francesco; Signorovitch, James; Sajeev, Gautam; Goemans, Nathalie; Wong, Brenda; Tian, Cuixia; Mercuri, Eugenio; Done, Nicolae; Wong, Hallee; Moss, Jackson; Yao, Zhiwen; Ward, Susan J.; Manzur, Adnan; Servais, Laurent; Niks, Erik H.; Straub, Volker; de Groot, Imelda JM; McDonald, Craig
In Neuromuscular Disorders April 2022 32(4):271-283
Academic Journal
Sawnani, Hemant; Horn, Paul S.; Wong, Brenda; Darmahkasih, Andrew; Rybalsky, Irina; Shellenbarger, Karen C.; Tian, Cuixia; Rutter, Meilan M.; Simakajornboon, Narong; Amin, Raouf; Gurbani, Neepa; Pascoe, John; Burrows, Carolyn; Khirani, Sonia; Amaddeo, Alessandro; Fauroux, Brigitte
In The Journal of Pediatrics July 2019 210:194-200
Academic Journal
In Journal of AAPOS June 2018 22(3):192-196
Academic Journal
Muntoni, Francesco; Signorovitch, James; Sajeev, Gautam; Lane, Henry; Jenkins, Madeline; Dieye, Ibrahima; Ward, Susan; Goemans, Nathalie; Niks, Erik; Wong, Brenda; Servais, Laurent; Straub, Volker; Guglieri, Michela; de Groot, Imelda; Chesshyre, Mary; Tian, Cuixia; Manzur, Adnan; Mercuri, Eugenio; Aartsma-Rus, Annemieke; McDonald, Craig
Neurology. 100(15)
Academic Journal
Marden, Jessica; Shieh, Perry; Wong, Brenda; Lane, Henry; Zhang, Adina; Nguyen, Ha; Frean, Molly; Trifillis, Panayiota; Koladicz, Karyn; Signorovitch, James; McDonald, Craig
Journal of Comparative Effectiveness Research. 12(4)
Academic Journal
Alfano, Lindsay N; Eagle, Michelle; James, Meredith K; Lowes, Linda; Mayhew, Anna; Mazzone, Elena S; Nelson, Leslie; Rose, Kristy J; Abdel-Hamid, Hoda Z; Apkon, Susan D; Barohn, Richard J; Bertini, Enrico; Bloetzer, Clemens; de Vaud, Lausanne Canton; Butterfield, Russell J; Chabrol, Brigitte; Chae, Jong-Hee; Jongno-gu, Daehak-ro; Comi, Giacomi Pietro; Darras, Basil T; Dastgir, Jahannaz; Desguerre, Isabelle; Escobar, Raul G; Finanger, Erika; Guglieri, Michela; Hughes, Imelda; Iannaccone, Susan T; Jones, Kristi J; Karachunski, Peter; Kudr, Martin; Lotze, Timothy; Mah, Jean K; Mathews, Katherine; Nevo, Yoram; Parsons, Julie; Péréon, Yann; de Queiroz Campos Araujo, Alexandra Prufer; Renfroe, J Ben; de Resende, Maria Bernadete Dutra; Ryan, Monique; Selby, Kathryn; Tennekoon, Gihan; Vita, Giuseppe; McDonald, Craig M; Campbell, Craig; Torricelli, Ricardo Erazo; Finkel, Richard S; Flanigan, Kevin M; Goemans, Nathalie; Heydemann, Peter; Kaminska, Anna; Kirschner, Janbernd; Muntoni, Francesco; Osorio, Andrés Nascimento; Schara, Ulrike; Sejersen, Thomas; Shieh, Perry B; Sweeney, H Lee; Topaloglu, Haluk; Tulinius, Már; Vilchez, Juan J; Voit, Thomas; Wong, Brenda; Elfring, Gary; Kroger, Hans; Luo, Xiaohui; McIntosh, Joseph; Ong, Tuyen; Riebling, Peter; Souza, Marcio; Spiegel, Robert J; Peltz, Stuart W; Mercuri, Eugenio
In The Lancet 23-29 September 2017 390(10101):1489-1498
Academic Journal
Johnson, Laurel L.; Phythian, Kelli; Wong, Brenda; McGill, Claire; Hinds, Aaliyah; Choate, Ellison; Zelcer, Hannah; Mendez, Eunice; Movahedi, Yasaman; Friedberg, Robert D.
Academic Journal
Rouillon, Jeremy; Zocevic, Aleksandar; Leger, Thibaut; Garcia, Camille; Camadro, Jean-Michel; Udd, Bjarne; Wong, Brenda; Servais, Laurent; Voit, Thomas; Svinartchouk, Fedor
In Neuromuscular Disorders July 2014 24(7):563-573
Academic Journal
Zichichi, Albert; Ammar, Mahmoud; Numbers, Bobbi; Zemaitis, Christopher; Sakya, Sagune; Wong, Brenda; Wallace, Ryan
Critical Care Medicine. Jan 01, 2024 52(1 Suppl 1):S658-S658
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