학술논문
3 - Lentiviral-Mediated Ex-Vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I): Interim Results from an Ongoing Phase 1/2 Study
Document Type
Abstract
Author
Booth, Claire; Sevilla, Julian; Rao, Gayatri; Lopez, Maria Chitty; Almarza, Elena; Terrazas, Dayna; Zubicaray, Josune; Gonzalez-Vicent, Marta; Chetty, Kritika; Xu-Bayford, Jinhua; O’Toole, Grainne; Fernandes, Augustine; Kuo, Caroline Y.; De Oliveira, Satiro N.; Mesa-Núñez, Cristina; Moore, Theodore B.; Nicoletti, Eileen; Choi, Grace; Zeini, Miriam; Thrasher, Adrian J.; Bueren, Juan; Schwartz, Jonathan; Kohn, Donald B.
Source
In Transplantation and Cellular Therapy February 2023 29(2) Supplement:S2-S3
Subject
Language
ISSN
2666-6367