학술논문
Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant
Document Type
Article
Author
McIntosh, Jenny; Lenting, Peter J.; Rosales, Cecilia; Lee, Doyoung; Rabbanian, Samira; Raj, Deepak; Patel, Nishil; Tuddenham, Edward G.D.; Christophe, Olivier D.; McVey, John H.; Waddington, Simon; Nienhuis, Arthur W.; Gray, John T.; Fagone, Paolo; Mingozzi, Federico; Zhou, Shang-Zhen; High, Katherine A.; Cancio, Maria; Ng, Catherine Y.C.; Zhou, Junfang; Morton, Christopher L.; Davidoff, Andrew M.; Nathwani, Amit C.
Source
In Blood 25 April 2013 121(17):3335-3344
Subject
Language
ISSN
0006-4971