학술논문
Lipid nanoparticle delivery limits antisense oligonucleotide activity and cellular distribution in the brain after intracerebroventricular injection
Document Type
Article
Author
Byrnes, Amy E.; Dominguez, Sara L.; Yen, Chun-Wan; Laufer, Benjamin I.; Foreman, Oded; Reichelt, Mike; Lin, Han; Sagolla, Meredith; Hötzel, Kathy; Ngu, Hai; Soendergaard, Christoffer; Estevez, Alberto; Lin, Hsiu-Chao; Goyon, Alexandre; Bian, Juan; Lin, Jessica; Hinz, Flora I.; Friedman, Brad A.; Easton, Amy; Hoogenraad, Casper C.
Source
In Molecular Therapy - Nucleic Acids 13 June 2023 32:773-793
Subject
Language
ISSN
2162-2531