학술논문
Maralixibat in progressive familial intrahepatic cholestasis (MARCH-PFIC): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
Document Type
Article
Author
Miethke, Alexander G ; Moukarzel, Adib; Porta, Gilda; Covarrubias Esquer, Joshue; Czubkowski, Piotr; Ordonez, Felipe; Mosca, Antonella; Aqul, Amal A; Squires, Robert H; Sokal, Etienne; D'Agostino, Daniel; Baumann, Ulrich; D'Antiga, Lorenzo; Kasi, Nagraj; Laborde, Nolwenn; Arikan, Cigdem; Lin, Chuan-Hao; Gilmour, Susan; Mittal, Naveen; Chiou, Fang Kuan; Horslen, Simon P; Huber, Wolf-Dietrich; Jaecklin, Thomas; Nunes, Tiago; Lascau, Anamaria; Longpre, Lara; Mogul, Douglas B; Garner, Will; Vig, Pamela; Hupertz, Vera F; Gonzalez-Peralta, Regino P; Ekong, Udeme; Hartley, Jane; Laverdure, Noemie; Ovchinsky, Nadia; Thompson, Richard J
Source
In The Lancet Gastroenterology & Hepatology July 2024 9(7):620-631
Subject
Language
ISSN
2468-1253